The Center for Rare Diseases focuses on new treatments for rare, ultra-rare and rare variants of common diseases.
Advancing Hope for Patients with Huntington's Disease
New Hope for Patients with Friedreich's Ataxia: The Promise of Omaveloxolone
2023 Rare Disease Day Webinar: Advancing Novel Therapies in Rare Diseases
Advancing A Novel Treatment for Rare Autoimmune Diseases
Webinar: Accelerating Cures in Rare Disease
Bringing New Hope to Families Living with Rare Disease
Webinar: Novel Treatments for Rare Neurological Diseases