The Center for Rare Diseases focuses on new treatments for rare, ultra-rare and rare variants of common diseases.
Harrington Discovery Institute Study Leads to Promise for Thirst Disorder Therapeutics
Advancing Hope for Patients with Huntington's Disease
New Hope for Patients with Friedreich's Ataxia: The Promise of Omaveloxolone
2023 Rare Disease Day Webinar: Advancing Novel Therapies in Rare Diseases
Advancing A Novel Treatment for Rare Autoimmune Diseases
Webinar: Accelerating Cures in Rare Disease
Bringing New Hope to Families Living with Rare Disease
Webinar: Novel Treatments for Rare Neurological Diseases