
February 28, 2026
Op-Ed Authored by Lord (David) Cameron, former UK Prime Minister and Chair of the OHC Advisory Council published in The Daily Telegraph on Saturday, Feb. 28, 2026 (Rare Disease Day) Rare diseases are not actually that rare. Collectively they affect 500 million people around the world. Some, such as Huntington’s disease...
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January 15, 2026
Prestigious Scholar Award Accelerates Novel Therapies for Patients with Rare Diseases Continue Reading
December 23, 2025
New Study from University Hospitals and Case Western Reserve University published in Science Signaling Continue Reading
December 22, 2025
For over a century, Alzheimer's disease (AD) has been considered irreversible. Consequently, research has focused on disease prevention or slowing, rather than recovery. Despite billions of dollars spent on decades of research, there has never been a clinical trial of a drug for AD with an outcome goal of reversing disease and... Continue Reading
November 20, 2025
Ten scientists selected for second annual award to pursue innovations in gene, RNA, small molecule and cell therapies to treat rare and ultra-rare diseases Continue Reading
November 13, 2025
Positive results at AHA Scientific Sessions, published in NEJM Evidence Continue Reading
October 15, 2025
Grant award provides MD/PhD candidates with funding and expertise to translate promising scientific discoveries into medicines Continue Reading
September 10, 2025
In ‘A Conversation on Courage,’ Lord Cameron and Morgan Stanley’s Andy Saperstein discussed philanthropy as a catalyst for rare disease innovation Continue Reading
June 24, 2025
Harrington Discovery Institute and the American Society for Clinical Investigation seek nominations to recognize an outstanding achievement by a physician-scientist Continue Reading
June 03, 2025
Drug development grant will advance 10 physician-scientists’ discoveries toward the clinic Continue Reading
May 23, 2025
Scientific researchers and leaders from across the globe gathered in Cleveland, Ohio to discuss progress being made in drug development for a variety of conditions, including Alzheimer’s and rare diseases. Continue Reading