June 24, 2025
National and international nominations are being sought for the 2026 Harrington Prize for Innovation in Medicine, which honors a physician-scientist who has moved science forward with achievements notable for innovation, creativity and the potential for clinical application. The Harrington Prize, which carries a $20,000...
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February 05, 2025
Award highlights collaboration between for profit and non-profit achieving great impact Continue Reading
January 27, 2025
At 18 weeks pregnant, Lindsey learned her baby had severe spina bifida. She joined UC Davis’s groundbreaking CuRe Trial combining fetal surgery and stem cells. Over a year later, her son is thriving. Continue Reading
January 15, 2025
Scholar Award Accelerates Novel Therapies for Rare Diseases Continue Reading
December 11, 2024
An off-the-shelf drug shows promise as a low-cost topical treatment for psoriasis. New findings highlight benzamil’s potential to reduce inflammation and skin cell overgrowth without steroids or immune suppression. Continue Reading
December 03, 2024
Inherited SP-B deficiency is an ultra-rare monogenic cause of fatal respiratory distress syndrome in newborn infants with few, if any, options for long-term survival Continue Reading
November 15, 2024
Oxford, UK – 15th November 2024 – (or ‘the Company’, www.alveogene.com), a company focused on transforming rare respiratory disease outcomes using inhaled gene therapy, announces that it has been granted a Rare Pediatric Disease Designation (RPDD) by the US Food & Drug Administration (FDA) for AVG-002, its novel... Continue Reading
October 24, 2024
10 scientists have been selected for OHC’s first annual award to advance academic discoveries into clinical practice for rare diseases Continue Reading
October 15, 2024
Lord Cameron will lead international efforts to drive the OHC’s mission of delivering 40 new therapies for rare diseases into clinical trials over the next ten years Continue Reading
September 26, 2024
Grant award provides MD/PhD candidates with funding and expertise to translate promising scientific discoveries into medicines Continue Reading