November 20, 2025
OXFORD, UK and CLEVELAND, Ohio, US, 20 November 2025 – The Oxford-Harrington Rare Disease Centre (‘OHC’) today announced the recipients of the 2025 Rare Disease Scholar Award, which advances promising discoveries from academic labs into clinical practice. Each Scholar will receive an advisory team providing...
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November 14, 2025
Scientists are trying a revolutionary new approach to treat rheumatoid arthritis, multiple sclerosis, lupus and other devastating autoimmune diseases — by reprogramming patients’ out-of-whack immune systems. Continue Reading
November 13, 2025
Positive results of zalunfiban announced at AHA Scientific Sessions Continue Reading
October 15, 2025
Grant award provides MD/PhD candidates with funding and expertise to translate promising scientific discoveries into medicines Continue Reading
September 10, 2025
In ‘A Conversation on Courage,’ Lord Cameron and Morgan Stanley’s Andy Saperstein discussed philanthropy as a catalyst for rare disease innovation Continue Reading
July 20, 2025
Published in Good News NetworkEleven years of cancer research has proven fruitful for a scientist at Johns Hopkins who uncovered a new tumor-suppressive response that could lead to novel therapies targeting hard-to-treat cancers.The new study, funded in part by the National Institutes of Health and the National Cancer... Continue Reading
July 09, 2025
Experimental Compound Offers Potential Treatment for Rare, Often Fatal, Childhood Disease Continue Reading
July 09, 2025
Published in NatureAbstractDecreased brain levels of coenzyme Q10 (CoQ10), an endogenously synthesized lipophilic antioxidant,, underpin encephalopathy in primary CoQ10 deficiencies, and are associated with common neurodegenerative diseases and the ageing process,. CoQ10 supplementation does not increase CoQ10 pools in the... Continue Reading
June 24, 2025
Harrington Discovery Institute and the American Society for Clinical Investigation seek nominations to recognize an outstanding achievement by a physician-scientist Continue Reading
June 19, 2025
Published in Cell Chemical BiologySignificanceEnzymes that regulate oncogenic protein function through the addition of post-translational modifications (PTMs) represent promising targets for the development of cancer therapeutics. N-glycosylation is a critical PTM that occurs in the lumen of the endoplasmic reticulum (ER) and... Continue Reading
June 04, 2025
The former prime minister has called for children admitted to paediatric care to undergo genome sequencing as part of a drive to cure 40 rare diseases Continue Reading