December 03, 2024
Inherited SP-B deficiency is an ultra-rare monogenic cause of fatal respiratory distress syndrome in newborn infants with few, if any, options for long-term survival Highly encouraging preclinical data highlight the possibility of lifelong treatment from a single administration of AVG-002 with preparations for clinical...
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October 03, 2023
The Therapeutics Accelerator will identify, fund and advance innovative projects from academic partners in the U.K. and U.S. with the goal to deliver 40 new potentially life-changing therapies for rare diseases into clinical trials over 10 years. Continue Reading
September 29, 2023
Aleta hopes to initiate the registrational trial investigating ALETA-001 in B-cell malignancies in 2024/25. Continue Reading
September 23, 2023
Agreement enables the development of therapeutics, including AcuraStem's AS-202 Candidate, an antisense oligonucleotide that suppresses levels of the PIKFYVE kinase Continue Reading
September 14, 2023
New gene therapy company created and funded by Oxford Science Enterprises, Harrington Discovery Institute and Old College Capital in partnership with six leading scientists from the world-renowned UK Respiratory Gene Therapy Consortium (GTC) Continue Reading
September 14, 2023
Cell therapies derived from stem cells could one day prevent vision loss or even restore sight in retinal degenerative disease. Continue Reading
August 22, 2023
A Conversation with Jonathan S. Stamler, MD, President of Harrington Discovery Institute Continue Reading
July 05, 2023
New Orleans, LA – LSU Health New Orleans today announced that has exercised its option to receive an exclusive license to certain early-stage technology designed to slow the progression of DNA repeat expansion disorders.In DNA repeat expansion disorders, a segment of repeated DNA expands within a gene to cause disease. The... Continue Reading
May 09, 2023
Harrington Discovery Institute and the American Society for Clinical Investigation seek nominations to recognize an outstanding achievement by a physician-scientist Continue Reading
May 01, 2023
Atsena Therapeutics announced that the FDA has cleared the company’s IND application for a Phase I/II clinical trial of ATSN-201 in patients with X-linked retinoschisis (XLRS), featuring Harrington Scholar Shannon Boye, PhD, University of Florida. Continue Reading
April 26, 2023
10 physician-scientists have been selected for drug development grant to advance discoveries into the clinic Continue Reading